Niemann-Pick Disease, A Pipeline Analysis Report 2018

Technavio has published a new report on the drug development pipeline for Niemann-pick disease, including a study of the pipeline molecules.

Lipid Management for the Prevention of Atherosclerotic Cardiovascular Disease

Niemann- Pick Disease Type C (NPC) Market Report 2023-2033 - Wissen Research

Cells, Free Full-Text

Orphazyme's arimoclomol to be used with Zavesca after FDA approval

Cureus, Niemann-Pick Disease: A Case Report and Literature Review

The Pipeline Report 2013: Late-Stage Standouts - MM+M - Medical Marketing and Media

Niemann-Pick disease type-B: a unique case report with compound heterozygosity and complicated lipid management, BMC Medical Genetics

Dysphagia as a risk factor for mortality in Niemann-Pick disease type C: systematic literature review and evidence from studies with miglustat, Orphanet Journal of Rare Diseases

Investigation of Brain Iron in Niemann-Pick Type C: A 7T Quantitative Susceptibility Mapping Study

Biomolecules, Free Full-Text

Global Niemann-Pick Disease Market and Competitive Landscape - 2021

PDF) Mass spectrometry imaging of lipids: untargeted consensus spectra reveal spatial distributions in Niemann-Pick disease type C1

An integrated multiomic approach as an excellent tool for the diagnosis of metabolic diseases: our first 3720 patients

The cholesterol transporter NPC1 is essential for epigenetic regulation and maturation of oligodendrocyte lineage cells