Niemann-Pick Disease, Types C1 (D)
Por um escritor misterioso
Last updated 22 setembro 2024
Tolerance of chronic HDACi treatment for neurological, visceral
Gene therapy shows promise for treating Niemann-Pick disease type
IJMS, Free Full-Text
Necroptosis in Niemann–Pick disease, type C1: a potential
Science Update: Biomarker for Niemann-Pick type C may be useful
Niemann-Pick disease type C
The Neuropsychiatry of Niemann-Pick Type C Disease in Adulthood
Understanding the phenotypic variability in Niemann-Pick disease
Recommendations for the detection and diagnosis of Niemann-Pick
mRNA Treatment Rescues Niemann–Pick Disease Type C1 in Patient
Critical role for glycosphingolipids in Niemann-Pick disease type
PDF] Niemann-Pick Disease Type C in Adulthood - A Psychiatric and
PDF) Recommendations on the diagnosis and management of Niemann
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