Walgreen's Support Allows Our Twins with Niemann Pick Type C To Receive Cyclodextrin Treatments At Home

We are sorry for the lack of posts in recent months! Hugh and I have been extremely busy with rare disease initiatives for Solution Therapeutics, our virtual biotech, as well as helping the Global Genes Project with a number of community based rare disease projects. We would like to report that after three years of

Parents of twins with Niemann-Pick find a treatment

Walgreens Collaborates with Curebase to Increase Diversity in

Gene Therapy Center at Casey Eye Institute

Intrathecal cyclodextrin in the treatment of Niemann-Pick disease

Two Newly-Approved Gene Therapies Cost Millions - DNA Science

A hopeful therapy for Niemann-Pick C diseases - The Lancet

Investigation of 2-Hydroxypropyl-β-Cyclodextrin Treatment in a

Tripledemic' Forces Pharmacies to Limit Purchases of Children's

Dynarex - Syringes With Needle - 3cc – GoBioMed

Walgreens Collaborates with Curebase to Increase Diversity in

Walgreens Collaborates with Curebase to Increase Diversity in

PDF) Lipid biology of the podocyte—New perspectives offer new