Strategies to combat Tay-Sachs disease - ScienceDirect

Efficient and precise generation of Tay–Sachs disease model in rabbit by prime editing system

Mutation Story – Tay-Sachs

Strategies to combat Tay-Sachs disease - ScienceDirect

Frontiers New Approaches to Tay-Sachs Disease Therapy

Spontaneous appearance of Tay–Sachs disease in an animal model - ScienceDirect

Neurological manifestations of lysosomal disorders and emerging therapies targeting the CNS - The Lancet Child & Adolescent Health

Targeting Ferroptosis: New Hope for As-Yet-Incurable Diseases: Trends in Molecular Medicine

Substrate Reduction Therapy for Sandhoff Disease through Inhibition of Glucosylceramide Synthase Activity: Molecular Therapy

Frontiers Therapeutic Strategies For Tay-Sachs Disease